The FDA is hosting a virtual public meeting to join the global observance of Rare Disease Day.

The theme for FDA’s Rare Disease Day is “Sharing Experiences in Rare Diseases Together.” This public meeting will include six interactive panel discussions. Panelists, including current and former FDA staff, patients and caregivers, will speak about their experiences in:
- Enhancing product development using a public-private partnership approach for a rare disease
- Reviewing gene therapies for neurocognitive disorders in children
- Engaging in review processes that led to approval of two drugs to treat rare tumors
- Using patient input and benefit-risk assessments in approval of devices for rare orthopedic conditions
- Interacting with FDA
- Developing initiatives to improve FDA’s work in rare diseases

Panel discussions will be moderated and allow panelists to provide individual perspectives. Panelists will be able to respond to attendee questions using a chat feature. Click for more information and registration