Clinical trials are an important part of drug development and must take place before a medicine can be approved for use as a drug prescribed by doctors. Read below to learn more about the phases of clinical trials and how new therapies become available to people who need them. To see definitions for terms used, visit the Clinical Trial Glossary page.
About Clinical Trials
Clinical trials are voluntary studies carried out in people to answer specific research questions. Clinical trials:
- Study the safety and effectiveness of new drugs or procedures
- Assess new ways of using existing treatments
- Can be designed to learn more about a disease (e.g. a
natural history study)
It’s important to know that:
- Clinical trials are not treatments; they are research studies. Participating in a clinical trial doesn’t mean that a drug will make your symptoms better or will stop the spread of a disease. You may even
get a placeboin a clinical trial that doesn’t help you at all.
- Many drugs have unwanted side effects that can range from mild to very serious or life-threatening. However, by participating in a clinical trial, you are helping researchers evaluate the safety and effectiveness of new drugs for FOP and answer important scientific questions.
The decision to participate in a clinical trial is yours. Participation is always voluntary, and you can withdraw from a clinical trial at any time.